How big is the rare diseases treatment industry?

The global rare diseases treatment market size is expected to increase USD 488.76 billion by 2033 from USD 205.70 billion in 2023. Read More

What is the growth rate of the rare diseases treatment industry?

The global rare diseases treatment market will register growth rate of 9.04% between 2024 and 2033. Read More

Who are the prominent players operating in the rare diseases treatment market?

The major players operating in the rare diseases treatment market are F. Hoffmann-La Roche Ltd., Pfizer, Inc., PTC Therapeutics, AstraZeneca, Novartis AG, Takeda Pharmaceutical Company, Bayer AG, AbbVie Inc., Merck & Co. Inc., Bristol Myers Squibb, and Others. Read More

Which are the driving factors of the rare diseases treatment market?

The driving factors of the rare diseases treatment market are the rapid FDA approvals of rare disease treatment boost the market and advancements in biotechnology and research. Read More

Which region will lead the global rare diseases treatment market?

North America region will lead the global rare diseases treatment market during the forecast period 2024 to 2033. Read More

Rare Diseases Treatment Market Size, Share, and Trends 2024 to 2033

Rare Diseases Treatment Market (By Drug Type: Biologics, Non-biologics; By Therapeutic Area: Cancer, Blood-Related Disorder, Central Nervous System, Respiratory Disorders, Musculoskeletal Disorders, Cardiovascular Disorder, Other Therapeutic Areas; By Patient: Adult, Pediatric; By Route of Administration: Oral, Injectable, Others; By Distribution Channel: Hospital Pharmacy, Specialty Pharmacy, Online Pharmacy) - Global Industry Analysis, Size, Share, Growth, Trends, Regional Outlook, and Forecast 2024-2033

Last Updated : June 2024
Report Code : 4410
Category : Healthcare

Chapter 1. Introduction

1.1. Research Objective

1.2. Scope of the Study

1.3. Definition

Chapter 2. Research Methodology (Premium Insights)

2.1. Research Approach

2.2. Data Sources

2.3. Assumptions & Limitations

Chapter 3. Executive Summary

3.1. Market Snapshot

Chapter 4. Market Variables and Scope

4.1. Introduction

4.2. Market Classification and Scope

4.3. Industry Value Chain Analysis

4.3.1. Raw Material Procurement Analysis

4.3.2. Sales and Distribution Channel Analysis

4.3.3. Downstream Buyer Analysis

Chapter 5. COVID 19 Impact on Rare Diseases Treatment Market

5.1. COVID-19 Landscape: Rare Diseases Treatment Industry Impact

5.2. COVID 19 - Impact Assessment for the Industry

5.3. COVID 19 Impact: Global Major Government Policy

5.4. Market Trends and Opportunities in the COVID-19 Landscape

Chapter 6. Market Dynamics Analysis and Trends

6.1. Market Dynamics

6.1.1. Market Drivers

6.1.2. Market Restraints

6.1.3. Market Opportunities

6.2. Porter’s Five Forces Analysis

6.2.1. Bargaining power of suppliers

6.2.2. Bargaining power of buyers

6.2.3. Threat of substitute

6.2.4. Threat of new entrants

6.2.5. Degree of competition

Chapter 7. Competitive Landscape

7.1.1. Company Market Share/Positioning Analysis

7.1.2. Key Strategies Adopted by Players

7.1.3. Vendor Landscape

7.1.3.1. List of Suppliers

7.1.3.2. List of Buyers

Chapter 8. Global Rare Diseases Treatment Market, By Drug Type

8.1. Rare Diseases Treatment Market, by Drug Type, 2024-2033

8.1.1. Biologics

8.1.1.1. Market Revenue and Forecast (2021-2033)

8.1.2. Non-biologics

8.1.2.1. Market Revenue and Forecast (2021-2033)

Chapter 9. Global Rare Diseases Treatment Market, By Therapeutic Area

9.1. Rare Diseases Treatment Market, by Therapeutic Area, 2024-2033

9.1.1. Cancer

9.1.1.1. Market Revenue and Forecast (2021-2033)

9.1.2. Blood-Related Disorder

9.1.2.1. Market Revenue and Forecast (2021-2033)

9.1.3. Central Nervous System

9.1.3.1. Market Revenue and Forecast (2021-2033)

9.1.4. Respiratory Disorders

9.1.4.1. Market Revenue and Forecast (2021-2033)

9.1.5. Musculoskeletal Disorders

9.1.5.1. Market Revenue and Forecast (2021-2033)

9.1.6. Cardiovascular Disorder

9.1.6.1. Market Revenue and Forecast (2021-2033)

9.1.7. Other Therapeutic Areas

9.1.7.1. Market Revenue and Forecast (2021-2033)

Chapter 10. Global Rare Diseases Treatment Market, By Patient

10.1. Rare Diseases Treatment Market, by Patient, 2024-2033

10.1.1. Adult

10.1.1.1. Market Revenue and Forecast (2021-2033)

10.1.2. Pediatric

10.1.2.1. Market Revenue and Forecast (2021-2033)

Chapter 11. Global Rare Diseases Treatment Market, By Route of Administration

11.1. Rare Diseases Treatment Market, by Route of Administration, 2024-2033

11.1.1. Oral

11.1.1.1. Market Revenue and Forecast (2021-2033)

11.1.2. Injectable

11.1.2.1. Market Revenue and Forecast (2021-2033)

11.1.3. Others

11.1.3.1. Market Revenue and Forecast (2021-2033)

Chapter 12. Global Rare Diseases Treatment Market, By Distribution Channel

12.1. Rare Diseases Treatment Market, by Distribution Channel, 2024-2033

12.1.1. Hospital Pharmacy

12.1.1.1. Market Revenue and Forecast (2021-2033)

12.1.2. Specialty Pharmacy

12.1.2.1. Market Revenue and Forecast (2021-2033)

12.1.3. Online Pharmacy

12.1.3.1. Market Revenue and Forecast (2021-2033)

Chapter 13. Global Rare Diseases Treatment Market, Regional Estimates and Trend Forecast

13.1. North America

13.1.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.1.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.1.3. Market Revenue and Forecast, by Patient (2021-2033)

13.1.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.1.5. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.1.6. U.S.

13.1.6.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.1.6.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.1.6.3. Market Revenue and Forecast, by Patient (2021-2033)

13.1.6.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.1.6.5. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.1.7. Rest of North America

13.1.7.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.1.7.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.1.7.3. Market Revenue and Forecast, by Patient (2021-2033)

13.1.7.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.1.7.5. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.2. Europe

13.2.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.2.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.2.3. Market Revenue and Forecast, by Patient (2021-2033)

13.2.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.2.5. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.2.6. UK

13.2.6.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.2.6.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.2.6.3. Market Revenue and Forecast, by Patient (2021-2033)

13.2.7. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.2.8. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.2.9. Germany

13.2.9.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.2.9.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.2.9.3. Market Revenue and Forecast, by Patient (2021-2033)

13.2.10. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.2.11. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.2.12. France

13.2.12.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.2.12.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.2.12.3. Market Revenue and Forecast, by Patient (2021-2033)

13.2.12.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.2.13. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.2.14. Rest of Europe

13.2.14.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.2.14.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.2.14.3. Market Revenue and Forecast, by Patient (2021-2033)

13.2.14.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.2.15. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.3. APAC

13.3.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.3.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.3.3. Market Revenue and Forecast, by Patient (2021-2033)

13.3.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.3.5. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.3.6. India

13.3.6.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.3.6.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.3.6.3. Market Revenue and Forecast, by Patient (2021-2033)

13.3.6.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.3.7. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.3.8. China

13.3.8.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.3.8.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.3.8.3. Market Revenue and Forecast, by Patient (2021-2033)

13.3.8.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.3.9. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.3.10. Japan

13.3.10.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.3.10.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.3.10.3. Market Revenue and Forecast, by Patient (2021-2033)

13.3.10.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.3.10.5. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.3.11. Rest of APAC

13.3.11.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.3.11.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.3.11.3. Market Revenue and Forecast, by Patient (2021-2033)

13.3.11.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.3.11.5. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.4. MEA

13.4.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.4.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.4.3. Market Revenue and Forecast, by Patient (2021-2033)

13.4.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.4.5. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.4.6. GCC

13.4.6.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.4.6.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.4.6.3. Market Revenue and Forecast, by Patient (2021-2033)

13.4.6.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.4.7. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.4.8. North Africa

13.4.8.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.4.8.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.4.8.3. Market Revenue and Forecast, by Patient (2021-2033)

13.4.8.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.4.9. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.4.10. South Africa

13.4.10.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.4.10.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.4.10.3. Market Revenue and Forecast, by Patient (2021-2033)

13.4.10.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.4.10.5. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.4.11. Rest of MEA

13.4.11.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.4.11.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.4.11.3. Market Revenue and Forecast, by Patient (2021-2033)

13.4.11.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.4.11.5. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.5. Latin America

13.5.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.5.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.5.3. Market Revenue and Forecast, by Patient (2021-2033)

13.5.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.5.5. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.5.6. Brazil

13.5.6.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.5.6.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.5.6.3. Market Revenue and Forecast, by Patient (2021-2033)

13.5.6.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.5.7. Market Revenue and Forecast, by Distribution Channel (2021-2033)

13.5.8. Rest of LATAM

13.5.8.1. Market Revenue and Forecast, by Drug Type (2021-2033)

13.5.8.2. Market Revenue and Forecast, by Therapeutic Area (2021-2033)

13.5.8.3. Market Revenue and Forecast, by Patient (2021-2033)

13.5.8.4. Market Revenue and Forecast, by Route of Administration (2021-2033)

13.5.8.5. Market Revenue and Forecast, by Distribution Channel (2021-2033)

Chapter 14. Company Profiles

14.1. F. Hoffmann-La Roche Ltd.

14.1.1. Company Overview

14.1.2. Product Offerings

14.1.3. Financial Performance

14.1.4. Recent Initiatives

14.2. Pfizer, Inc.

14.2.1. Company Overview

14.2.2. Product Offerings

14.2.3. Financial Performance

14.2.4. Recent Initiatives

14.3. PTC Therapeutics

14.3.1. Company Overview

14.3.2. Product Offerings

14.3.3. Financial Performance

14.3.4. Recent Initiatives

14.4. AstraZeneca

14.4.1. Company Overview

14.4.2. Product Offerings

14.4.3. Financial Performance

14.4.4. Recent Initiatives

14.5. Novartis AG

14.5.1. Company Overview

14.5.2. Product Offerings

14.5.3. Financial Performance

14.5.4. Recent Initiatives

14.6. Takeda Pharmaceutical Company

14.6.1. Company Overview

14.6.2. Product Offerings

14.6.3. Financial Performance

14.6.4. Recent Initiatives

14.7. Bayer AG

14.7.1. Company Overview

14.7.2. Product Offerings

14.7.3. Financial Performance

14.7.4. Recent Initiatives

14.8. AbbVie Inc.

14.8.1. Company Overview

14.8.2. Product Offerings

14.8.3. Financial Performance

14.8.4. Recent Initiatives

14.9. Merck & Co. Inc.

14.9.1. Company Overview

14.9.2. Product Offerings

14.9.3. Financial Performance

14.9.4. Recent Initiatives

14.10. Bristol Myers Squibb

14.10.1. Company Overview

14.10.2. Product Offerings

14.10.3. Financial Performance

14.10.4. Recent Initiatives

Chapter 15. Research Methodology

15.1. Primary Research

15.2. Secondary Research

15.3. Assumptions

Chapter 16. Appendix

16.1. About Us

16.2. Glossary of Terms

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Rare Diseases Treatment Market Size to Hit USD 488.76 Bn by 2033

List of Contents